Modelling and simulation of experimental designs to find the best design of randomized clinical trials in a rare disease: Cystic fibrosis

P. Kurbatova, A. Bajard, H. Tiddens, V. Volpert, C. Cornu, N. Bessonov, B. Kassai, S. Chabaud, P. Nony, D. Caudri (Lyon, Bron, France; Rotterdam, Netherlands)

Source: International Congress 2014 – Cystic fibrosis: clinical assessment and treatment
Session: Cystic fibrosis: clinical assessment and treatment
Session type: Thematic Poster Session
Number: 1220
Disease area: Paediatric lung diseases

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P. Kurbatova, A. Bajard, H. Tiddens, V. Volpert, C. Cornu, N. Bessonov, B. Kassai, S. Chabaud, P. Nony, D. Caudri (Lyon, Bron, France; Rotterdam, Netherlands). Modelling and simulation of experimental designs to find the best design of randomized clinical trials in a rare disease: Cystic fibrosis. Eur Respir J 2014; 44: Suppl. 58, 1220

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