In vivo genome editing using nuclease-encoding mRNA corrects SP-B deficiency
Alexander Dewerth (Tübingen, Germany), Alexander Dewerth, Azita Mahiny, Lauren E. Mays, Mohammed Alkahled, Benedikt Mothes, Emad Malaeksefat, Brigitta Loretz, Jennifer Rottenberger, Darina M. Brosch, Philipp Reautschnig, Pacharapan Surapolchai, Franziska Zeyer, Andrea Schams, Melanie Carevic, Martina Bakele, Matthias Griese, Matthias Schwab, Bernd Nürnberg, Sandra Beer-Hammer, Rupert Handgretinger, Dominik Hartl, Claus-Michael Lehr, Michael S.D. Kormann
Source: International Congress 2016 – Molecular targets in pulmonary disease
Session: Molecular targets in pulmonary disease
Session type: Thematic Poster
Number: 889
Disease area: Airway diseases
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Alexander Dewerth (Tübingen, Germany), Alexander Dewerth, Azita Mahiny, Lauren E. Mays, Mohammed Alkahled, Benedikt Mothes, Emad Malaeksefat, Brigitta Loretz, Jennifer Rottenberger, Darina M. Brosch, Philipp Reautschnig, Pacharapan Surapolchai, Franziska Zeyer, Andrea Schams, Melanie Carevic, Martina Bakele, Matthias Griese, Matthias Schwab, Bernd Nürnberg, Sandra Beer-Hammer, Rupert Handgretinger, Dominik Hartl, Claus-Michael Lehr, Michael S.D. Kormann. In vivo genome editing using nuclease-encoding mRNA corrects SP-B deficiency. Eur Respir J 2016; 48: Suppl. 60, 889
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