Access to medicines for rare diseases: beating the drum for primary ciliary dyskinesia

Suzanne Crowley, Inês Azevedo, Mieke Boon, Andrew Bush, Ernst Eber, Eric Haarman, Bulent Karadag, Karsten Kötz, Margaret Leigh, Antonio Moreno-Galdó, Huda Mussaffi, Kim G. Nielsen, Heymut Omran, Jean-François Papon, Petr Pohunek, Kostas Priftis, Bernhard Rindlisbacher, Francesca Santamaria, Arunas Valiulis, Michal Witt, Panayiotis Yiallouros, Zorica Zivkovic, Claudia E. Kuehni, Jane S. Lucas

Source: ERJ Open Res, 6 (3) 00377-2020; 10.1183/23120541.00377-2020

Journal Issue: July

Disease area: Paediatric lung diseases

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Suzanne Crowley, Inês Azevedo, Mieke Boon, Andrew Bush, Ernst Eber, Eric Haarman, Bulent Karadag, Karsten Kötz, Margaret Leigh, Antonio Moreno-Galdó, Huda Mussaffi, Kim G. Nielsen, Heymut Omran, Jean-François Papon, Petr Pohunek, Kostas Priftis, Bernhard Rindlisbacher, Francesca Santamaria, Arunas Valiulis, Michal Witt, Panayiotis Yiallouros, Zorica Zivkovic, Claudia E. Kuehni, Jane S. Lucas. Access to medicines for rare diseases: beating the drum for primary ciliary dyskinesia. ERJ Open Res, 6 (3) 00377-2020; 10.1183/23120541.00377-2020

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