Source: Eur Respir Monogr 2014; 64: 129-149
Disease area: Paediatric lung diseases



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Isabelle Sermet-Gaudelus, Jacques de Blic, Muriel LeBourgeois, Iwona Pranke, Aleksander Edelman, Bonnie W. Ramsey. Potentiating and correcting mutant CFTR in patients with cystic fibrosis. Eur Respir Monogr 2014; 64: 129-149

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