A helper-dependent adenoviral vector rescues CFTR to wild-type functional levels in cystic fibrosis epithelial cells harbouring class I mutations

Huibi Cao, Hong Ouyang, Onofrio Laselva, Claire Bartlett, Zhichang Peter Zhou, Cathleen Duan, Tarini Gunawardena, Julie Avolio, Christine E. Bear, Tanja Gonska, Jim Hu, Theo J. Moraes

Source: Eur Respir J, 56 (5) 2000205; 10.1183/13993003.00205-2020
Journal Issue: November

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Huibi Cao, Hong Ouyang, Onofrio Laselva, Claire Bartlett, Zhichang Peter Zhou, Cathleen Duan, Tarini Gunawardena, Julie Avolio, Christine E. Bear, Tanja Gonska, Jim Hu, Theo J. Moraes. A helper-dependent adenoviral vector rescues CFTR to wild-type functional levels in cystic fibrosis epithelial cells harbouring class I mutations. Eur Respir J, 56 (5) 2000205; 10.1183/13993003.00205-2020

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