Rare pulmonary diseases and orphan drugs: where do we stand and where are we going to?

Harari Sergio, Humbert Marc, Blasi Francesco, Collard Harold R., Matucci-Cerinic Marco, Simonneau Gerald, Vancheri Carlo, Wells Athol U., Cottin Vincent

Source: Eur Respir Rev 2015; 24: 375-377
Journal Issue: September

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Harari Sergio, Humbert Marc, Blasi Francesco, Collard Harold R., Matucci-Cerinic Marco, Simonneau Gerald, Vancheri Carlo, Wells Athol U., Cottin Vincent. Rare pulmonary diseases and orphan drugs: where do we stand and where are we going to?. Eur Respir Rev 2015; 24: 375-377

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